DUBLIN, Oct. 18, 2019 /PRNewswire/ -- The "Fanconi Anemia (FA) - Pipeline Insight, 2019" drug pipelines has been added to ResearchAndMarkets.com's offering. Fanconi Anemia (FA) - Pipeline Insight, ...

“ We have now dosed 11 Fanconi Anemia patients and have at least 12-months of follow-up on eight of these patients in our clinical trial of RP-L102. In six of these eight patients, we see evidence of ...

Gene therapies could have a major impact, although the cost and complexities could inhibit their wide rollout, study authors said. New advancements in gene therapy and hematopoietic stem cell ...

The rare disease Fanconi anemia is an inherited bone marrow disorder linked to birth defects that leads to failure of bone marrow, the spongy material inside the bones where stem cells develop.

Experts at Cincinnati Children's have uncovered striking metabolic differences in people with Fanconi anemia (FA), a rare genetic disorder that causes bone marrow failure and dramatically increases ...

Anemia poses a significant public health challenge, primarily impacting the health of young children, pregnant and postpartum women, as well as menstruating adolescent girls and adult women. On a ...

Combining Ixazomib With Subcutaneous Rituximab and Dexamethasone in Relapsed or Refractory Waldenström's Macroglobulinemia: Final Analysis of the Phase I/II HOVON124/ECWM-R2 Study We identified 421 ...

The Fanconi Anemia pathway, named after a cancer-predisposition syndrome, is essential for the repair of DNA-interstrand crosslinks (ICLs). The pathway consists of 22 FA complementation group proteins ...

Mutations in FANCX appear to cause a lethal form of Fanconi anemia, a finding that sheds light on unexplained pregnancy loss and offers new avenues for genetic screening. Fanconi anemia is an ...

Rocket Pharmaceuticals (NASDAQ:RCKT) announced on Thursday that it will reduce its workforce by about 30% as part of a restructuring effort. This decision, along with other planned cost-saving ...