Bright Minds Biosciences has debuted glowing phase 2 results for its lead anti-seizure asset, giving the biotech’s stock a ...
BMB-101 demonstrated significant anti-seizure benefit in both cohorts with favorable safety and tolerability Absence: 73.1% ...
The trial had 24 patients, exceeding the original target of 20, and included a 4-week baseline. ・In the Absence cohort, ...
Dosed First Patient in REVEAL Pivotal Trial in the Fourth Quarter of 2025. Additional enrollment continues to advance across ...
REVEAL Phase 1/2 Adolescent and Adult Trial (Canada and U.S.): a first-in-human, open-label, randomized, dose-escalation and dose-expansion study evaluating the safety and preliminary efficacy of TSHA ...
A UC San Diego lab recently announced a pair of scientific breakthroughs for Pitt-Hopkins and Rett syndromes that are slated ...
Rett syndrome is one of the rare genetic disorders and almost exclusively affects girls. In Germany, an estimated 5,000 people are affected, with about 50 new cases each year. A disturbing sign: After ...
Richard Engel tells PEOPLE that a recent effect of son Henry's condition has been the fact that he's "starting to have seizures now, which is unfortunate" Charlotte Triggs is a digital leader and ...
The investigational drug trofinetide showed modest benefit in girls and young women with Rett syndrome, the phase III LAVENDER study showed. After 12 weeks of treatment, significant differences in two ...
Dr. Katherine Loveland answers the question: 'What Is Rett Syndrome?' Oct. 23, 2008 -- Question: What is Rett syndrome? Answer: Rett syndrome is a neurodevelopmental disorder in which a child develops ...
In Rett syndrome, a genetic condition affecting girls almost exclusively, mutations in the MECP2 gene cause a regression of language and motor skills starting at 12 to 18 months of age. Children then ...
SRF (SYNGAP1), RSRT (Rett), CACNA1A, STXBP1, Loulou (CDKL5), & KCNQ2 Cure (KCNQ2) collaborate to support Dr. Devinsky’s research for clinical trial readiness. Co-funded by multiple organizations, this ...