"BioMarin’s trial for phenylketonuria therapy meets primary efficacy endpoint" was originally created and published by Clinical Trials Arena, a GlobalData owned brand. The information on this ...

Alexa Beichler's boys were born with classic phenylketonuria (PKU), a metabolic condition that requires them to be on medical-grade formula for life Anya Leon is a Senior News Editor and the ...

Synthetic biology specialist Synlogic will start phase 3 testing of a drug for rare metabolic disorder phenylketonuria (PKU) next year, after reporting solid proof-of-concept data. PKU is a rare ...

Considering taking supplements to treat phenylketonuria pku? Below is a list of common natural remedies used to treat or reduce the symptoms of phenylketonuria pku. Follow the links to read common ...

has issued a positive opinion for Sephience for the treatment of phenylketonuria, an inherited genetic disorder. The New Drug Application (NDA) for sepiapterin is under review by the U.S. Food and ...

Cycle Pharmaceuticals (Cycle) has launched Cycle Vita PKU, an AI-powered app to help patients with PKU manage every aspect of ...

PEGASUS is a Phase 3 multi-center open-label randomized controlled study evaluating the safety and efficacy of PALYNZIQ compared to diet alone in 55 adolescents aged 12-17 with phenylketonuria.

Pegvaliase statistically significantly lowered blood Phe levels in adolescents with PKU compared with diet alone. Topline data were announced from a phase 3 trial evaluating pegvaliase-pqpz in ...

Cycle Pharmaceuticals (Cycle) has launched Cycle Vita PKU, an AI-powered app to help patients with PKU manage every aspect of their treatment plan. It can be challenging for patients with PKU, or ...