In the phase 1/2 INSPIRE DUCHENNE trial, data from the first 3 patients dosed revealed an average microdystrophin expression of 110%, as measured by western blot, and improvements in multiple ...

A 13-year-old female with a history of iron deficiency anemia presented with altered mental status preceded by 5 days of headache, vomiting, nausea, and worsening somnolence that was not responsive to ...

On March 26, 2025, the new drug application (NDA) for diazoxide choline extended-release tablets (VYKAT XR; Soleno Therapeutics) was approved by the FDA to treat hyperphagia among individuals aged 4 ...

Recent research detailed that a child was most likely to be killed in a mass shooting by a parent or family member vs a stranger or peer. Study investigator Stephanie Chao, MD, breaks down these data.

A new clinical trial has found that omalizumab (Xolair; Genetech, Novartis) is more effective than oral immunotherapy (OIT) in treating multi-food allergy in individuals with severe allergic reactions ...

Can you diagnose this patient? Take our poll and find out! Then check back for the full case, differential diagnosis, and correct diagnosis. Welcome to this Contemporary Pediatrics poll. Take a look ...

The approval marks a vital step toward care for urinary tract infections, helping to reduce recurrence and improve patients’ quality of life. The FDA has approved gepotidacin (Blujepa; GSK), for use ...

Tina Tan, MD, FIDSA, FPIDS, FAAP, comments on the FDA's recent selection of the 2025-2026 influenza vaccine compositions, without the CDC's ACIP meeting and FDA's VRBPAC meeting. On March 13, 2025, ...

In 2021, the American Academy of Pediatrics, American Academy of Child and Adolescent Psychiatry, and the Children’s Hospital Association jointly declared a national emergency in child and adolescent ...

A healthy 9-year-old girl developed an asymptomatic eruption of discrete and confluent, 2 to 3 mm, hypopigmented papules in a linear pattern along the lines of Blaschko on the back of her left thigh ...

Pediatric cancer survivors can be vulnerable to cardiovascular disease in the short- or long-term with increased recognition of cardiotoxic cancer treatments, as 5-year survival rates for children are ...

With 1 in 7 adolescents worldwide diagnosed with mental health disorders, emerging research suggests that diet is a powerful yet often overlooked therapeutic tool. Adolescence brings a perfect storm ...