Sarepta Therapeutics | Biopharmaceutical Company for Rare …
Sarepta is engineering solutions for rare diseases with science that is on the forefront of precision genetic medicine. Our platforms include: gene therapy, RNA technologies, and gene editing. …
About Our Company - Sarepta Therapeutics
Sarepta is a global biotechnology company on an urgent mission: to engineer precision genetic medicine for rare diseases that devastate lives and cut futures short.
Our Pipeline | Sarepta Therapeutics
Jun 27, 2024 · Sarepta’s industry leading pipeline is comprised of over 40 programs in various stages of development across 3 technologies, RNA, gene therapy and gene editing, and …
Meet Our Leadership | Sarepta Therapeutics
Learn about Sarepta's leadership and their goal to forever change the course of genetic disease.
News & Press Releases - Sarepta Therapeutics
Read news and articles from Sarepta, a global biotechnology company developing potentially life-changing precision genetic medicine.
The Science Behind Our Precision Genetic Medicine Platforms
Sarepta is pursuing the development of precision genetic medicine at the forefront of biotechnology for rare diseases: gene therapy, RNA-targeted exon skipping, and gene editing. …
Duchenne Muscular Dystrophy (DMD) | Sarepta Therapeutics
Sarepta currently has multiple clinical trials for Duchenne underway in both gene therapy and RNA exon-skipping.
Our Disease Areas - Sarepta Therapeutics
At Sarepta, we’re committed to pursuing some of the world’s most debilitating, prevalent, and complex rare genetic diseases. Today, our primary focus is on Duchenne muscular dystrophy, …
Sarepta Therapeutics Announces FDA Approval of ELEVIDYS, the …
Jun 22, 2023 · Sarepta is responsible for global development and manufacturing for ELEVIDYS, and distribution within the U.S. will commence immediately. In December 2019, Sarepta …
Pipeline & Products | Sarepta Therapeutics
Sarepta is at the forefront of precision genetic medicine, with over 40 therapies in various stages of development. Our disease areas include Duchenne muscular dystrophy (DMD), six Limb …